Associated Papers
Clinical and Genetic Re-Evaluation of Inherited Retinal Degeneration Pedigrees following Initial Negative Findings on Panel-Based Next Generation Sequencing.
Stephenson KAJ et al.
International Journal of Molecular Sciences, 2022
A gene therapeutic approach to correct splice defects with modified U1 and U6 snRNPs.
Schmid F et al.
Human Gene Therapy, 2013
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