Associated Papers
Precision Editing as a Therapeutic Approach for β-Hemoglobinopathies.
Paschoudi K et al.
International Journal of Molecular Sciences, 2023
In vivo HSPC gene therapy with base editors allows for efficient reactivation of fetal γ-globin in β-YAC mice.
Li C et al.
Blood Advances, 2021
Manipulation of Developmental Gamma-Globin Gene Expression: an Approach for Healing Hemoglobinopathies.
Venkatesan V et al.
Molecular and Cellular Biology, 2020
The Effect of Five Single Nucleotide Polymorphisms on Hb F Variation of β-Thalassemia Traits and Hematologically Normal Individuals in Southeast Turkey.
Genc A et al.
Hemoglobin, 2020
Natural regulatory mutations elevate the fetal globin gene via disruption of BCL11A or ZBTB7A binding.
Martyn GE et al.
Nature Genetics, 2018
The relevance of hemoglobin F measurement in the diagnosis of thalassemias and related hemoglobinopathies.
Mosca A et al.
Clinical Biochemistry, 2009
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