Associated Papers
Unraveling the Mechanism of Action, Binding Sites, and Therapeutic Advances of CFTR Modulators: A Narrative Review.
Baroni D
Current Issues in Molecular Biology, 2025
One Size Does Not Fit All: The Past, Present and Future of Cystic Fibrosis Causal Therapies.
Ensinck MM et al.
Cells, 2022
CFTR modulator therapy for cystic fibrosis caused by the rare c.3700A>G mutation.
Phuan PW et al.
Journal of Cystic Fibrosis : Official Journal of the European Cystic Fibrosis Society, 2021
1-BENZYLSPIRO[PIPERIDINE-4,1'-PYRIDO[3,4-b]indole] 'co-potentiators' for minimal function CFTR mutants.
Son JH et al.
European Journal of Medicinal Chemistry, 2021
Nanomolar-potency 'co-potentiator' therapy for cystic fibrosis caused by a defined subset of minimal function CFTR mutants.
Phuan PW et al.
Scientific Reports, 2019
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