Associated Papers
CRISPR for cystic fibrosis: Advances and insights from a systematic review.
Nicosia L et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy, 2025
A streamlined base editor engineering strategy to reduce bystander editing.
Valdez I et al.
Nature Communications, 2025
Use of adenine base editing and homology-independent targeted integration strategies to correct the cystic fibrosis causing variant, W1282X.
Mention K et al.
Human Molecular Genetics, 2023
Functional correction of CFTR mutations in human airway epithelial cells using adenine base editors.
Krishnamurthy S et al.
Nucleic Acids Research, 2021
On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis.
Ensinck M et al.
Frontiers in Pharmacology, 2021
Chemical modifications of adenine base editor mRNA and guide RNA expand its application scope.
Jiang T et al.
Nature Communications, 2020
Mutations in SELENBP1, encoding a novel human methanethiol oxidase, cause extraoral halitosis.
Pol A et al.
Nature Genetics, 2018
29255262 (PubMed )
Supplement: NIHMS74866-supplement-Supplementary_table_1.xlsx › EXAC_CFTR
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