Associated Papers
ACE-tRNAs are a platform technology for suppressing nonsense mutations that cause cystic fibrosis.
Ko W et al.
Nucleic Acids Research, 2025
Optimization of ACE-tRNAs function in translation for suppression of nonsense mutations.
Porter JJ et al.
Nucleic Acids Research, 2024
Efficient suppression of endogenous CFTR nonsense mutations using anticodon-engineered transfer RNAs.
Ko W et al.
Molecular Therapy. Nucleic Acids, 2022
Nanomolar-potency 'co-potentiator' therapy for cystic fibrosis caused by a defined subset of minimal function CFTR mutants.
Phuan PW et al.
Scientific Reports, 2019
Identification of the amino acids inserted during suppression of CFTR nonsense mutations and determination of their functional consequences.
Xue X et al.
Human Molecular Genetics, 2017
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