Associated Papers
Suppressor tRNAs as personalized therapy for nonsense mutation-associated pathologies.
Ignatova Z et al.
Pharmacology & Therapeutics, 2025
Efficient exon skipping by base-editor-mediated abrogation of exonic splicing enhancers.
Qiu H et al.
Cell Reports, 2023
Large scale population screening for Duchenne muscular dystrophy-Predictable and unpredictable challenges.
Cohen G et al.
Prenatal Diagnosis, 2022
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