Associated Papers
Exploring gene editing as a potential therapeutic strategy for hemophilia.
Kumarasamy N et al.
Frontiers in Bioengineering and Biotechnology, 2026
Targeted B-domain deletion restores F8 function in human endothelial cells and mice.
Hu Z et al.
Signal Transduction and Targeted Therapy, 2022
ssODN-Mediated In-Frame Deletion with CRISPR/Cas9 Restores FVIII Function in Hemophilia A-Patient-Derived iPSCs and ECs.
Hu Z et al.
Molecular Therapy. Nucleic Acids, 2019
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