Associated Papers
Defective autophagy and increased apoptosis contribute toward the pathogenesis of FKRP-associated muscular dystrophies.
Ortiz-Cordero C et al.
Stem Cell Reports, 2021
34653404 (PubMed )
Supplement: mmc1.pdf
A universal gene correction approach for FKRP-associated dystroglycanopathies to enable autologous cell therapy.
Dhoke NR et al.
Cell Reports, 2021
Global FKRP Registry: observations in more than 300 patients with Limb Girdle Muscular Dystrophy R9.
Murphy LB et al.
Annals of Clinical and Translational Neurology, 2020
32342672 (PubMed )
Supplement: ACN3-7-757-s001.pdf
Select a paper to view details