Associated Papers
Neutral sp2-iminosugars exploiting non-glycone interactions for selective acid α- and β-glucosidase activity modulation: Pharmacological chaperones for Gaucher and Pompe diseases.
García-Moreno MI et al.
European Journal of Medicinal Chemistry, 2026
Therapeutic Role of Pharmacological Chaperones in Lysosomal Storage Disorders: A Review of the Evidence and Informed Approach to Reclassification.
Keyzor I et al.
Biomolecules, 2023
37627292 (PubMed )
Supplement: biomolecules-13-01227-s001.zip › biomolecules-2489010-supplementary.pdf
The pharmacological chaperone effect of N-octyl-beta-valienamine on human mutant acid beta-glucosidases.
Luan Z et al.
Blood Cells, Molecules & Diseases, 2010
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