Associated Papers
A GLB1 transgene with enhanced therapeutic potential for the preclinical development of ex-vivo gene therapy to treat mucopolysaccharidosis type IVB.
Crippa S et al.
Molecular Therapy. Methods & Clinical Development, 2024
Promoter recognition by a complex of Spx and the C-terminal domain of the RNA polymerase alpha subunit.
Nakano MM et al.
Plos One, 2010
Select a paper to view details