Associated Papers
Efficacy and safety of miglustat in the treatment of GM2 gangliosidosis: A systematic review.
Mansouri V et al.
European Journal of Neurology, 2023
Natural History of Adult Patients with GM2 Gangliosidosis.
Masingue M et al.
Annals of Neurology, 2020
New cases of adult-onset Sandhoff disease with a cerebellar or lower motor neuron phenotype.
Delnooz CC et al.
Journal of Neurology, Neurosurgery, and Psychiatry, 2010
Substrate reduction therapy in juvenile GM2 gangliosidosis.
Maegawa GH et al.
Molecular Genetics and Metabolism, 0
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