Associated Papers
Splice-switching antisense oligonucleotides correct cryptic exon inclusion and restore SDCCAG8 protein in Bardet-Biedl Syndrome.
McEntee KE et al.
Biorxiv : the Preprint Server for Biology, 2025
41279107 (PubMed )
Supplement: NIHPP2025.10.15.682674v1-supplement-1.pdf
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