Associated Papers
A protein domain-oriented approach to expand the opportunities of therapeutic exon skipping for USH2A-associated retinitis pigmentosa.
Schellens RTW et al.
Molecular Therapy. Nucleic Acids, 2023
Antisense oligonucleotide-based treatment of retinitis pigmentosa caused by USH2A exon 13 mutations.
Dulla K et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy, 2021
Clinical and preclinical therapeutic outcome metrics for USH2A-related disease.
Toms M et al.
Human Molecular Genetics, 2020
Usherin defects lead to early-onset retinal dysfunction in zebrafish.
Dona M et al.
Experimental Eye Research, 2018
Pathogenesis and Treatment of Usher Syndrome Type IIA.
Zaw K et al.
Asia-pacific Journal of Ophthalmology (philadelphia, Pa.), 0
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